Holders — by stockHoldings — by fund
Palo Alto Investors LP
Everything this manager disclosed owning in US-listed stocks — its complete Form 13F portfolio · as of 2026-06-30 · filed with the SEC up to 45 days after quarter end · CIK 0001306923
$723.7M
disclosed book value
52
positions
10.4%
largest position share
Positions, as of 2026-06-30
top 52 of 52 · 13F covers long US-listed positions only — cash, bonds, private and foreign stakes are not disclosed · PUT/CALL tags = options positions (share-equivalents), not shares held
| # | Issuer | Shares | Value | % of book |
|---|---|---|---|---|
| 1 | PTCTPTC THERAPEUTICS INC | 918,846 | $75.0M | 10.4% |
| 2 | ACADACADIA PHARMACEUTICALS INC | 2.9M | $72.5M | 10% |
| 3 | INSMINSMED INC | 413,980 | $44.1M | 6.1% |
| 4 | MIRMMIRUM PHARMACEUTICALS INC | 348,808 | $40.8M | 5.6% |
| 5 | ANABANAPTYSBIO INC | 603,489 | $40.7M | 5.6% |
| 6 | BMRNBIOMARIN PHARMACEUTICAL INC | 682,777 | $39.1M | 5.4% |
| 7 | DYNDYNE THERAPEUTICS INC | 1.6M | $36.6M | 5.1% |
| 8 | UTHRUNITED THERAPEUTICS CORP | 62,587 | $33.9M | 4.7% |
| 9 | IRONDISC MEDICINE INC | 416,646 | $30.5M | 4.2% |
| 10 | BIIBBIOGEN INC | 140,279 | $30.3M | 4.2% |
| 11 | IOVAIOVANCE BIOTHERAPEUTICS INC | 5.3M | $22.0M | 3% |
| 12 | RAREULTRAGENYX PHARMACEUTICAL IN | 596,495 | $19.9M | 2.8% |
| 13 | NOVOCURE LTD | 1.3M | $19.4M | 2.7% |
| 14 | SNDXSYNDAX PHARMACEUTICALS INC | 864,986 | $18.9M | 2.6% |
| 15 | ANNXANNEXON INC | 2.9M | $16.8M | 2.3% |
| 16 | BCAXBICARA THERAPEUTICS INC | 550,408 | $16.3M | 2.3% |
| 17 | CDNACAREDX INC | 531,870 | $15.2M | 2.1% |
| 18 | CLDXCELLDEX THERAPEUTICS INC | 399,856 | $14.9M | 2.1% |
| 19 | CMPXCOMPASS THERAPEUTICS INC | 5.8M | $12.8M | 1.8% |
| 20 | ALKERMES PLC | 242,560 | $12.7M | 1.8% |
| 21 | TRAXFIRST TRACKS BIOTHERAPEUTICS | 603,489 | $12.1M | 1.7% |
| 22 | PROTHENA CORP PLC | 1.1M | $11.2M | 1.5% |
| 23 | TVTXTRAVERE THERAPEUTICS INC | 167,525 | $9.5M | 1.3% |
| 24 | TSHATAYSHA GENE THERAPIES INC | 1.4M | $9.5M | 1.3% |
| 25 | ACRSACLARIS THERAPEUTICS INC | 1.6M | $8.5M | 1.2% |
| 26 | AGIOAGIOS PHARMACEUTICALS INC | 213,601 | $7.9M | 1.1% |
| 27 | CAPRCAPRICOR THERAPEUTICS INC | 229,763 | $5.5M | 0.8% |
| 28 | ALGNALIGN TECHNOLOGY INC | 31,389 | $5.3M | 0.7% |
| 29 | ORKAORUKA THERAPEUTICS INC - Restricted | 33,546 | $3.2M | 0.4% |
| 30 | XENEXENON PHARMACEUTICALS INC | 51,345 | $3.1M | 0.4% |
| 31 | NBIXNEUROCRINE BIOSCIENCES INC | 18,117 | $3.1M | 0.4% |
| 32 | EWEDWARDS LIFESCIENCES CORP | 33,640 | $3.0M | 0.4% |
| 33 | STOKSTOKE THERAPEUTICS INC | 84,631 | $2.8M | 0.4% |
| 34 | CYTKCYTOKINETICS INC | 32,195 | $2.7M | 0.4% |
| 35 | PYXSPYXIS ONCOLOGY INC | 864,277 | $2.6M | 0.4% |
| 36 | EHTHEHEALTH INC | 1.5M | $2.2M | 0.3% |
| 37 | CRISPR THERAPEUTICS AG | 39,605 | $2.2M | 0.3% |
| 38 | SGMTSAGIMET BIOSCIENCES INC-A | 250,000 | $1.9M | 0.3% |
| 39 | NUVBNUVATION BIO INC | 326,609 | $1.9M | 0.3% |
| 40 | BNTXBIONTECH SE-ADR | 19,614 | $1.8M | 0.3% |
| 41 | CMPSCOMPASS PATHWAYS PLC ADR | 115,616 | $1.6M | 0.2% |
| 42 | HUMHUMANA INC | 3,985 | $1.6M | 0.2% |
| 43 | NEWAMSTERDAM PHARMA CO NV | 44,359 | $1.5M | 0.2% |
| 44 | VSTMVERASTEM INC | 309,685 | $1.2M | 0.2% |
| 45 | MDGLMADRIGAL PHARMACEUTICALS INC | 1,787 | $959,530 | 0.1% |
| 46 | UROGEN PHARMA LTD | 24,500 | $901,600 | 0.1% |
| 47 | BCYCBICYCLE THERAPEUTICS PLC-ADR | 201,890 | $856,014 | 0.1% |
| 48 | XERSXERIS BIOPHARMA HOLDINGS INC | 104,410 | $826,927 | 0.1% |
| 49 | ABEOABEONA THERAPEUTICS INC | 108,865 | $672,786 | 0.1% |
| 50 | INSPINSPIRE MEDICAL SYSTEMS INC | 8,772 | $391,319 | 0.1% |
| 51 | PROQR THERAPEUTICS NV | 188,807 | $351,181 | 0% |
| 52 | ALDXALDEYRA THERAPEUTICS INC | 155,709 | $331,660 | 0% |
Source: SEC Form 13F-HR, reporting period 2026-06-30. Values are the manager's filed June-30-style quarter-end marks, not live prices. Research, not investment advice.